AIDS virus used in gene therapy to fix ‘bubble baby’ disease
A gene therapy that makes use of an unlikely helper, the AIDS virus, gave a working immune system to 48 babies and toddlers who were born without one, doctors reported …
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Listen: Vaccine riches, patent waivers, & a gene therapy for aging
What does $45 billion buy you these days? Is clinical trial tourism a business? And will no one think of the patents? We cover all that and more this week …
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Six patients with dementia went to Mexico for an unproven gene therapy, a biotech CEO claims
Six patients with dementia traveled to Mexico last year to be injected with a gene therapy not authorized for use in the U.S., according to the CEO of a Seattle-area …
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HHS to prioritize newborn screening programs’ pipette tip orders
Programs that screen newborns for potentially deadly genetic conditions will now have higher priority when ordering pipette tips — a critical laboratory supply that is in shortage. STAT highlighted the …
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Opinion: Looking back at 15 years of sharing viral genomes to forge ahead
Anniversaries represent an opportunity for revisiting the past to make a leap forward. I’m using a 15-year anniversary of an act of scientific rebellion that changed my life — and …
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Huntington’s community grieves not just one therapeutic setback, but two
For the community of people affected by Huntington’s disease — a group that is no stranger to disappointment — the back-to-back announcements last month still hit like a double whammy. …
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Virtual Event: What gene-targeted therapies mean for patients with cancer
Editors note: A livestream of the event will be embedded below at 1 p.m. ET. Targeted treatments for cancers with specific mutations have dramatically changed the lives of some people …
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Opinion: To stem the pandemic, the U.S. needs a national Covid-19 genomic sequencing effort
More than a year into the pandemic, the United States is at yet another critical inflection point. The number of Covid-19 cases remains high and is on the rise in …
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Opinion: Listen: Walter Isaacson on CRISPR rivals and a Covid truce
In this week’s episode of STAT’s “First Opinion Podcast,” I talk with journalist, historian, and author Walter Isaacson about his First Opinion, “CRISPR rivals put patents aside to help in …
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